WCVB Channel 5 Boston: Gene therapy research offers hope for kids with Hirschsprung disease FIGHTING TO GET BETTER TREATMENT OPTIONS FOR A RARE CHILDHOOD CONDITION. IT’S CALLED HIRSCHSPRUNG DISEASE. THE EARLIEST SIGN IN A NEWBORN IS OFTEN CONSTIPATION.
THERE ARE TREATMENTS AVAILABLE. HERE’S ... Business Wire: The EMA Grants Orphan Drug Designation to Neurenati’s NEU-001 for the Treatment of Hirschsprung Disease The EMA Grants Orphan Drug Designation to Neurenati’s NEU-001 for the Treatment of Hirschsprung Disease Business Wire: Neurenati Therapeutics Concludes a 1.2 Million $ Seed Financing Round to Develop NEU-001 as a Promising Therapy for Hirschsprung Disease Neurenati Therapeutics Concludes a 1.2 Million $ Seed Financing Round to Develop NEU-001 as a Promising Therapy for Hirschsprung Disease Hirschsprung's disease (HSCR) and anorectal malformations (ARM) comprise a spectrum of congenital disorders that affect the distal gastrointestinal tract. HSCR is typified by aganglionosis, the ...
hirschsprung's disease, Neurenati Therapeutics Inc.’s NEU-001 has been awarded U.S. orphan drug and rare pediatric disease designations by the FDA for the treatment of Hirschsprung disease.
